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RecruitingLast updated: 22 June 2026

The ANZHIT-2 study: A study recruiting blood cancers that have a high risk of relapse to assess different immuno-suppressing treatment regimens prior to a stem cell transplantA multi-centre phase II, Australian and New Zealand, exploratory study of amendments to conditioning regimens in haplo-identical stem cell transplantation

Trial purpose

Medical clipboardCancer treatment

Tumor type

Blood Cancers Haematological

Age

People16 - 75

Trial acronym

The ANZHIT-2 study

Clinical summary

Summary

People who have been diagnosed with a blood cancer that has a risk of relapse, (e.g. Acute Myeloid Leukemia, Myeloid Dysplastic Syndrome, Chronic Myeloid Leukemia, Acute Lymphoblastic Leukemia, Hodgkin's Lymphoma or Non-Hodgkin's Lymphoma) may benefit from having a transplant of healthy stem cells into their bone marrow to encourage their body to produce healthy cells.

This treatment has a high risk of transplant rejection and so patients often need to take immuno-suppressing drugs for a time before and after the transplant to ensure the transplant is not rejected.

This study aims to assess 4 different immuno-suppressing treatment regimes (drugs and body irradiation/radiotherapy) to determine which treatment is best at suppressing the rejection response without compromising the overall health of the patient.

Who is it for?
You may be eligible for this study if you are aged 16 to 75 years of age, you have been diagnosed with a blood cancer that has a risk of relapse and your doctor has recommended that a stem cell transplant is indicated. You may also need to meet additional criteria (heart, lung and kidney health criteria) in order to be eligible for this study.

Study details
Participants in this study will take part in one of two separate sub-studies. The decision of which of the two sub-studies a participant will take part in is at the discretion of the study investigator. The two sub-studies are:

1. Reduced Intensity Conditioning (RIC) -Sub-study 1:  contains two sequential treatment arms. The first treatment arms.will examine using will use standard of care radiation but at a higher dose with fludarabine.  The second treatment arm will use of treosulfan instead of standard of care busulfan with fludarabine. Patients will have scans and blood tests before and after the transplant. Medical review will occur daily whilst in hospital and then once discharged as medically required (may start weekly then monthly)  

2 Myeloablative Conditioning (MAC) - Sub-study 2: contains 2 treatment arms running concurrently. One will use of treosulfan instead of standard of care busulfan with fludarabine and the other will use standard of care radiation but at a higher dose.  Patients will have scans and blood tests before and after the transplant. Medical review will occur daily whilst in hospital and then once discharged as medically required ( may start weekly then monthly)  

It is hoped this research will demonstrate that one (or many) of the treatment regimes tested is safe for cancer patients and effective at keeping the transplant rejection response rate low. The best treatment regime may then be tested in a larger randomised trial that could benefit future patients with blood cancers.

Conditions

This trial is treating people with blood cancers with a high risk of relapse

Eligibility

Inclusion

• Informed written consent.
• Patients 16 to 75 years of age
• Recipients must have a haematological malignancy with a significant risk of relapse (as measured by the Disease Risk Index13 (validated stratification system where allogeneic transplant is indicated).
• Adults without a matched related or unrelated donor or where the time for the donor cells to arrive places the patient at a high risk of relapse.
• Patients must have a first-degree relative who are 3out of 6 to 4out of 6 HLA matched (i.e. haploidentical)
• Adequate cardiac (LVEF greater than 50%), pulmonary (DLCO/VA greater than 50%) and renal function (Creatinine Clearance greater than 60ml per min).
• Patients with creatinine clearance between 41 to less than 60 ml per min will be assessed by their treating transplant specialist and if deemed suitable, can enrolled into the study.
• Haematological malignancies may be (but are not limited to):
- Acute Myeloid Leukemia (with high risk cytogenetics/mutations) in first complete remissionAMLCR1 (high risk cytogenetics or mutations),
- Acute Myeloid Leukemia (with high risk cytogenetics) in second complete remission
- Acute Myeloid Leukemia (with refractory disease with at least 2 adverse risk factors as per Centre for International Blood and Marrow Transplant Research.
- transformed Acute Myeloid Leukemia/Myeloid Dysplastic Syndrome
- Myeloid Dysplastic Syndrome with Intermediate level 2 as per International Prognostic Score System IPSS Int-2
- Myeloid Dysplastic Syndrome with high risk as per International Prognostic Score System
- Myeloproliferative Disease - eligible for HSCT – High DIPSS
_ Chronic Myeloid Leukemia with inadequate response to treatment
- Chronic Myeloid Leukemia in second chronic phase (CML prior Accelerated Phase or Blast Transformation)
- Acute Lymphoblastic Leukemia (with high risk cytogenetics) in first complete remission
- Acute Lymphoblastic Leukemia (with Minimal Residual Disease) in first complete remission
- Acute Lymphoblastic Leukemia in second complete response
- Hodgkin's Lymphoma in remission
- Non-Hodgkin's Lymphoma in remission

Exclusion

 

• Pregnancy.
• Positive serology for HIV.
• Refractory Central Nervous System (CNS) disease.
• Refractory lymphoma
• Serious organ dysfunction: LVEF less than 50%, FEV1, FVC, DLCO less than 50% of predicted, LFT greater than 5 times the upper limit of normal, or creatinine clearance less than 40 ml per min.
• Life expectancy less than 60 days.
• Unable or unwilling to provide written informed consent
• Previous adverse reaction to the treosulfan, fludarabine or cyclophosphamide
• Has any other clinically important abnormalities as determined by the investigator that may interfere with his or her participation in or compliance with the study.
• Presence of any psychological, familial, sociological or geographical condition potentially hampering compliance with the study protocol and follow-up schedule. This condition must be discussed with the patient prior to signing consent and registration in the trial.
• Prior Allogeneic stem cell transplant

Inclusion

  • You have had a certain type of treatment or surgical procedure.
  • You have the type of cancer, symptoms, or health risks that this clinical trial is focused on.

Exclusion

  • You have certain types of non-cancer medical conditions.
  • You have had certain treatments, surgical procedures or drugs.
Message

Clinical trials have complex eligibility criteria, and other criteria may apply for this trial. Ask your doctor about whether this trial could be right for you.

Participating hospitals

Recruiting hospitals

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More information

Trial Identifiers

Information on this page is partially produced from ANZCTR *. View further details about this trial on the registry via the links below:

Trial sponsor

St Vincent's Hospital, Sydney

Scientific Title

A multi-centre phase II, Australian and New Zealand, exploratory study of amendments to conditioning regimens in haplo-identical stem cell transplantation

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